Translation of MicroRNA-Based Huntingtin-Lowering Therapies from Preclinical Studies to the Clinic: Molecular Therapy
Synthetically Engineered Adeno-Associated Virus for Efficient, Safe, and Versatile Gene Therapy Applications | ACS Nano
High Levels of Persistent Expression of α1-Antitrypsin Mediated by the Nonhuman Primate Serotype rh.10 Adeno-associated Virus Despite Preexisting Immunity to Common Human Adeno-associated Viruses: Molecular Therapy
Terminal N-Linked Galactose Is the Primary Receptor for Adeno-associated Virus 9* - Journal of Biological Chemistry
Choroid plexus hAPP(SwInd) expression decreases proliferation in... | Download Scientific Diagram
VIRAL DELIVERY OF GDNF PROMOTES FUNCTIONAL INTEGRATION OF HUMAN STEM CELL GRAFTS IN PARKINSON'S DISEASE | bioRxiv
HI loop comparison of various AAV serotypes and autonomous... | Download Scientific Diagram
PDF) AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington's Disease Minipig Model
Soft subdermal implant capable of wireless battery charging and programmable controls for applications in optogenetics | Nature Communications
The AAV vector toolkit: poised at the clinical crossroads. - Abstract - Europe PMC
Science Magazine - November 29, 2019 - Median raphe controls acquisition of negative experience in the mouse
Molecular and neural basis of pleasant touch sensation | Science
Relevance of Assembly-Activating Protein for Adeno-associated Virus Vector Production and Capsid Protein Stability in Mammalian and Insect Cells | Journal of Virology
Surface Loop Dynamics in Adeno-Associated Virus Capsid Assembly | Journal of Virology
Generation of Cell Lines Capable of Producing High-titer Viral Stocks for Use in Vaccine Manufacture and Gene Therapy | ATCC
Rapid Highly-Efficient Digestion and Peptide Mapping of Adeno-Associated Viruses | Analytical Chemistry
Adeno-associated virus vectors for human gene therapy
Adeno-associated virus vectors for human gene therapy
Restoring brain cholesterol turnover improves autophagy and has therapeutic potential in mouse models of spinocerebellar ataxia
WO2020172490A1 - Recombinant adeno-associated virus for treatment of grn-associated adult-onset neurodegeneration - Google Patents
Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction w
Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction w
Synthetically Engineered Adeno-Associated Virus for Efficient, Safe, and Versatile Gene Therapy Applications | ACS Nano
